Medications for Fabry Disease

3 results

  • Elfabrio

    (pegunigalsidase alfa)
    Chiesi USA, Inc.
    Usage: ELFABRIO is indicated for the treatment of adults with confirmed Fabry disease.

  • Fabrazyme

    (AGALSIDASE BETA)
    Genzyme Corporation
    Usage: FABRAZYME® is indicated for the treatment of adult and pediatric patients aged 2 years and older who have confirmed Fabry disease.

  • Galafold

    (migalastat hydrochloride)
    Amicus Therapeutics US, LLC
    Usage: GALAFOLD is indicated for treating adults with a confirmed diagnosis of Fabry disease and an amenable GLA gene variant. The indication is based on accelerated approval following a reduction in kidney interstitial capillary cell globotriaosylceramide (KIC GL-3) substrate. Continued approval may require further clinical benefit verification.