Medications for Fabry Disease
3 results
Elfabrio (pegunigalsidase alfa)
(pegunigalsidase alfa)Chiesi USA, Inc.
Usage: ELFABRIO is indicated for the treatment of adults with confirmed Fabry disease, a genetic disorder that affects various bodily systems due to a deficiency in the enzyme alpha-galactosidase A.
Fabrazyme (agalsidase beta)
(AGALSIDASE BETA)Genzyme Corporation
Usage: FABRAZYME® is indicated for treating adult and pediatric patients aged 2 years and older with confirmed Fabry disease.
Galafold (migalastat hydrochloride)
(migalastat hydrochloride)Amicus Therapeutics US, LLC
Usage: GALAFOLD is indicated for treating adults with a confirmed diagnosis of Fabry disease who have an amenable GLA gene variant. Its approval is based on its ability to reduce kidney interstitial capillary cell globotriaosylceramide (KIC GL-3) substrates, with continued approval dependent on further clinical trials.