Medications for Glycogen Storage Disease Type Ii
3 results
Lumizyme (alglucosidase alfa)
(ALGLUCOSIDASE ALFA)Genzyme Corporation
Usage: LUMIZYME® is indicated for the treatment of Pompe disease, which is caused by acid α-glucosidase (GAA) deficiency.
Nexviazyme (avalglucosidase alfa)
(avalglucosidase alfa)Genzyme Corporation
Usage: NEXVIAZYME is indicated for treating late-onset Pompe disease in patients aged 1 year and older, specifically for those with lysosomal acid alpha-glucosidase (GAA) deficiency.
Pombiliti (cipaglucosidase alfa-atga)
(cipaglucosidase alfa-atga)AMICUS THERAPEUTICS US, LLC
Usage: POMBILITI, in combination with Opfolda, is indicated for adult patients weighing ≥40 kg with late-onset Pompe disease (GAA deficiency) who have not shown improvement on current enzyme replacement therapy (ERT).