Medications for Mucopolysaccharidosis Iv

1 result
  • vimizim - elosulfase alfa injection, solution, concentrate

    (Elosulfase Alfa)
    Biomarin Pharmaceutical Inc.
    Vimizim (elosulfase alfa) is indicated for patients with Mucopolysaccharidosis type IVA (MPS IVA; Morquio A syndrome).