Medications for Spinal Muscular Atrophy

6 results

  • Estradiol (estradiol)

    (estradiol)
    Preferred Pharmaceuticals Inc.
    Usage: Estradiol transdermal system is indicated for treating moderate to severe vasomotor symptoms and vulvar/vaginal atrophy due to menopause, hypoestrogenism from various causes, and preventing postmenopausal osteoporosis, ideally after evaluating other treatment options first.

  • Estradiol transdermal system (estradiol)

    (Estradiol)
    Sandoz Inc
    Usage: The Estradiol Transdermal System is indicated for treating moderate to severe vasomotor symptoms and vulvar/vaginal atrophy due to menopause, hypoestrogenism from various causes, and prevention of postmenopausal osteoporosis, with specific limitations for certain conditions.

  • Estring (estradiol)

    (estradiol)
    Pfizer Laboratories Div Pfizer Inc
    Usage: ESTRING is indicated for treating moderate to severe vulvar and vaginal atrophy symptoms associated with menopause.

  • Evrysdi

    (Risdiplam)
    Genentech Inc.
    Usage: EVRYSDI is indicated for the treatment of spinal muscular atrophy (SMA) in both pediatric and adult patients.

  • Spinraza

    (Nusinersen)
    Biogen
    Usage: SPINRAZA is indicated for the treatment of spinal muscular atrophy (SMA) in both pediatric and adult patients.

  • Zolgensma

    (onasemnogene abeparvovec-xioi)
    Novartis Gene Therapies, Inc.
    Usage: ZOLGENSMA is a gene therapy indicated for pediatric patients under 2 years old with spinal muscular atrophy (SMA) caused by bi-allelic mutations in the SMN1 gene. Its safety and effectiveness for repeat doses and in advanced SMA cases are not established.