Medications for Spinal Muscular Atrophy

3 results
  • spinraza - nusinersen injection, solution

    (Nusinersen)
    Biogen Inc.
    SPINRAZA treats spinal muscular atrophy (SMA) in pediatric and adult patients.
  • zolgensma - onasemnogene abeparvovec - xioi

    (Onasemnogene Abeparvovec-Xioi)
    Novartis Gene Therapies, Inc.
    Zolgensma is a gene therapy for pediatric patients under 2 years old with spinal muscular atrophy (SMA) caused by bi-allelic mutations in the SMN1 gene.